Amicus Pompe Disease Combo’s Approvability In Question As Key Trial Misses Mark

Company Touts ‘Totality Of Data’ As Supporting Approval

 
• By Alaric DeArment
Render illustration of Clinical Trial title on medical documents
Amicus' Phase III study of AT-GAA in Pompe disease failed to meet its primary endpoint, raising questions about the combination's approval prospects. • Source: Shutterstock

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