Drisapersen Advisory Committee Is Rough Welcome To FDA For Patient Groups

Advocates counter FDA’s problems with Duchenne muscular dystrophy treatment's trial data using real-life experience.

Spirits were not necessarily high among Duchenne muscular dystrophy patients and advocates heading into FDA’s advisory committee meeting on BioMarin Pharmaceutical Inc.’s drisapersen.

After reviewing FDA’s largely negative meeting briefing document, many of the attendees at the Nov. 24 Peripheral and Central Nervous...

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