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Patients Can't Rescue Sarepta's Eteplirsen

 
• By Derrick Gingery

Hours of testimony was clearly compelling, but advisory committee agreed with FDA concerns about the Duchenne muscular dystrophy drug's efficacy.

FDA advisory committee members were being pushed toward recommending approval of Sarepta Therapeutics Inc.'s eteplirsen during hours of testimony from patients on April 25, but in the end panelists had too many concerns about the design of the pivotal study.

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