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Exonics Using CRISPR To Develop One-Time Treatment for Duchenne

 
• By Brenda Sandburg

Newly formed biotech company hopes to avoid patent melee and use gene editing technology to develop therapy for up to 80% of boys with DMD; trial outcomes to drive terms of future licensing deals.

Abstract render of earth inside a glowing DNA strand ( earth uv map from http://visibleearth.nasa.gov )

Exonics Therapeutics Inc. aims to carve out a niche in the gene editing space with an approach that could potentially correct the underlying cause of Duchenne muscular dystrophy in up to 80% of boys with the disease.

The newly formed biotech company announced its launch on Feb. 27 with $5m in seed funding from CureDuchenne Ventures LLC....

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