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Sickle Cell Gene Therapy May Need New US-Backed Payment Program, Grogan Suggests

 
• By Cathy Kelly

Former senior advisor to President Trump warns that failure to reform drug pricing practices has seriously handicapped prospects for reimbursing cell and gene therapy under existing US payer programs.

DNA
Major Reimbursement Challenges Ahead For Gene Therapy

Reimbursement for upcoming high-cost cell and gene therapies may need to be handled by government-supported disease specific programs, former US Domestic Policy Council director Joe Grogan suggests, and he say sickle cell disease would be a good candidate for such an initiative.

In a speech to the American Society of Gene and Cell Therapy Policy Summit on 25 September, Grogan painted a somber picture of the reimbursement challenges facing the field.

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