The US Food and Drug Administration closed out last week with the approvals of two novel agents for rare diseases, Travere Therapeutics, Inc.'s Filspari for IgA nephropathy and Chiesi Global Rare Diseases’ Lamzede in alpha-mannosidosis.
Keeping Track: Travere’s Filspari, Chiesi’s Lamzede, Apellis’ Syfovre Headline US FDA Approvals; CRLs For Phathom, Biocon
The latest drug development news and highlights from the Pink Sheet’s US FDA Performance Tracker.
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