Companies Reveal Hurdles In Providing Drugs Via Expanded Access Programs

GSK, Stealth BioTherapeutics and Blueprint Medicines discuss the difficulties getting participation of physicians, the excessive cost of expanded access, and whether physicians should report research data.

Expanded access
Biopharma companies describe challenges in expanding access to investigational drugs • Source: Shutterstock

Experts in expanded access programs gave a glimpse of the difficulties in getting investigational drugs to patients, from helping physicians navigate the process to budgeting funds to pay for the programs.

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