PROFNAIT: Collaborating To Combat Rare Disease

Prophylix Pharma is set to be the first company to begin clinical trials for a prophylactic for fetal and neonatal alloimmune thrombocytopenia, a rare but serious disorder that can cause serious bleeding in babies' brains. Its candidate, NAITgam, is being developed under the auspices of the PROFNAIT consortium, an innovative collaborative project involving 11 Northern European universities, hospitals, research organizations, companies, and blood banks.

Norway-based Prophylix Pharma AS is set to be the first company to begin clinical trials for a prophylactic for FNAIT (fetal and neonatal alloimmune thrombocytopenia), a rare but serious disorder that affects around one in 2,000 pregnancies and can cause serious bleeds in babies' brains.

Prophylix's candidate NAITgam uses specific immunoglobulins from women who have previously given birth to a child affected by FNAIT to...

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