Sarepta Must Balance Exondys 51 Confirmatory Trials And Sales

How will the confirmatory trial necessary to convert accelerated approval to full approval affect sales given the small size of the target population?

Sarepta Therapeutics Inc.'s post-marketing requirements and sales efforts for Exondys 51 may wind up with conflicting and potentially opposite goals.

Now that the Duchenne muscular dystrophy treatment, the first approved by FDA, is ready to come on the market, patients surely will flock

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