Awaiting data from its pivotal APPROACH trial during the first quarter of 2017, Akcea Therapeutics was encouraged by safety and efficacy data unveiled Dec. 19 for lead candidate volanesorsen from a separate Phase III study in patients with severe hypertriglyceridemia, including a subset of patients with familial chylomicronemia syndrome (FCS).
Akcea, a subsidiary of antisense-focused Ionis Pharmaceuticals Inc., hopes to file volanesorsen for FCS in 2017 and plans a subsequent filing down the road in familial partial lipodystrophy (FPL),...
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