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Rett Syndrome Drug Could Propel Newron To Next Level In 2018

 
• By Lucie Ellis-Taitt

Newron Pharmaceuticals will file its investigational drug sarizotan in 2018 for respiratory issues in patients with Rett syndrome, setting it up to be the first therapy specifically indicated for this rare genetic disease. CEO Stefan Weber spoke to Scrip about Newron's commercial strategy for sarizotan and broader prospects for the evolving drug developer.

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Next Level: Newron is ready to expand if Rett syndrome drug is approved • Source: Shutterstock

Newron Pharmaceuticals SPA will target its second drug approval in 2018 – following on from the success of its partnered Parkinson's disease therapy Xadago (safinamide) – but this time the company is focused on a pediatric rare disease that could change its commercial prospects dramatically.

CEO Stefan Weber told Scrip that the company is leading research and development of new treatments for Rett syndrome, a rare genetic disorder that affects young girls, and expects to file its drug sarizotan in the US and Europe next year

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