APOLLO Success Clears Alnylam For Lift-Off

Phase III APOLLO results finally give the beleagured firm the first late-stage success for an RNAi thereapeutic and potentially a strong lead in the rare hereditary disease. 

train fast run on railway track in sunny day

Alnylam Pharmaceuticals Inc. finally reached the event the company and its investors had been waiting for – the receipt of positive Phase III data for its RNAi candidate patisiran in transthyretin-modulated amyloidosis polyneuropathy – and the company as well as its shareholders greeted it exuberantly.

Alnylam CEO John Maraganore said during a Sept. 20 call to unveil the APOLLO study's top-line results that, “Frankly, we...

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