Cell And Gene Therapies: Where Few Standard Rules Apply

Manufacturing, distribution and pricing challenges for cell and gene therapies have been mostly hypothetical – until now. But with no industry standards, the first products to win approval are dictating the complex path forward.

Machinery cogwheels, industry concept

The main rule of the cell and gene therapy market is there are few hard and fast rules when it comes to how to manufacture, distribute, administer and price these potentially curative treatments for cancer and rare diseases.

Without a standard set of rules agreed to by the therapies' developers, the first companies with approved products – along...

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