Global Blood Takes HOPE In Sickle Cell After Pulmonary Fibrosis Failure

GBT440 is not efficacious enough in studies of idiopathic pulmonary fibrosis, but the drug was well-tolerated at twice the exposure in the treatment of sickle cell disease, the drug's lead indication.

Sickle cell anemia, 3D illustration showing blood vessel with normal and deformated crescent-like red blood cells

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