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Alnylam Enjoys Autumn in Paris With hATTR Win Over Ionis

 
• By Kevin Grogan

Patisiran data impresses more than inotersen but Ionis is the first to file with a European submission.

Paris
Both Alnylam and Ionis seek to be top of the tree in hATTR • Source: Shutterstock

Alnylam Pharmaceuticals Inc.'s patisiran seems to be on course to become the standard of care for hereditary ATTR (hATTR) amyloidosis after the full data set from the APOLLO study on the first RNAi therapeutic to succeed in a late-stage trial were unveiled to acclaim at a conference in Paris.

In September, the top-line results from the APOLLO study led to a 52% leap in Alnylam's share price and the...

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