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Ultragenyx Gets Commercial Feet Wet With Mepsevii Launch In Sly Syndrome

 
• By Emily Hayes

Commercial opportunity for Mepsevii is small, but launch paves way for company's second product burosumab, following on its heels.

Rocket takes off from the hand of the businessman. Concept of start up.

Ultragenyx Pharmaceutical Inc.is planning to launch its first drug Mepsevii for the rare genetic disease Mucopolysaccharidosis VII, also called Sly syndrome, in the US with a lean commercial effort, while simultaneously planning for the introduction of its second product burosumab, which is currently under review.

The US FDA approved Mepsevii (vestronidase alfa-vjbk), a recombinant version of the enzyme beta-glucuronidase, for the treatment of

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