Summit DMD Data Intrigue But Longer-Term Results Awaited

Early data for ezutromid in Duchenne muscular dystrophy product give some proof of concept as a broad treatment for the fatal genetic disease – more data are awaited as Summit steps up its pivotal trial plans.

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Early Signs Of Efficacy For DMD Drug • Source: Shutterstock

Summit Therapeutics PLC's investigational drug candidate for Duchenne muscular dystrophy (DMD) ezutromid has reduced muscle damage in patients at the 24-week point in an ongoing Phase II trial, but the real test of the utrophin modulator's efficacy will come with the top-line results due in the third quarter of 2018.

Nonetheless, shares in Summit rose by nearly 13% to close at $13.78 on Nasdaq on Jan. 25 as investors digested the product's potential. Summit said the combination of reduced muscle...

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