Pfizer Inc. may have an unexpected blockbuster opportunity on its hands, as it reported significant cardiovascular outcomes data March 29 from a Phase III study of tafamidis meglumine in transthyretin-mediated cardiomyopathy. Approved overseas as Vyndaqel, tafamidis has been tied up since 2012 at US FDA for the related indication of familial amyloid polyneuropathy (FAP).
Pfizer May Enjoy Blockbuster Cardiomyopathy Success With Tafamidis
Although tafamidis has been stalled at FDA for transthyretin-mediated polyneuropathy, Pfizer may have found a different path toward US approval with cardiovascular outcomes data in cardiomyopathy.
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Pipeline Watch is a weekly snapshot of selected late-stage clinical trial events and approvals announced by pharmaceutical and biotech companies at medical and industry conferences, in financial and company presentations, and in company releases and statements.
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