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Ultragenyx Gets Second Drug Approval; Crysvita With Kyowa Hakko Kirin

 
• By Mandy Jackson

Ultragenyx already has a sales team in place to market its second commercial drug Crysvita (burosumab) – partnered with Kyowa Hakko Kirin – following its April 17 FDA approval for the treatment of pediatric and adult patients with x-linked hypophosphatemia (XLH).

FDA Approved typed words on a vintage typewriter

Crysvita (burosumab), approved in the US for the treatment of x-linked hypophosphatemia (XLH) – a rare, inherited form of rickets – on April 17, is Ultragenyx Pharmaceutical Inc.'s second drug to reach the market, but this time around the company has a commercial team already in place and a partner.

Crysvita follows Ultragenyx's Mepsevii (vestronidase alfa-vjbk) onto the market five months after the recombinant version of the enzyme beta-glucuronidase won US FDA approval for the treatment of the rare genetic disease Mucopolysaccharidosis VII (MPS VII), also known as Sly syndrome

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