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Amicus To See If Its Fabry Drug Galafold Can Benefit From Mis-Diagnosed MS

 
• By Sten Stovall

Rare disease specialist Amicus Therapeutics' lead product Galafold has recently launched with early success and the company's president tells Scrip further momentum could come from better Fabry disease diagnosis.

Occupational therapy
Amicus to target multiple sclerosis centers as Fabry can be mis-diagnosed as MS. • Source: Shutterstock

Amicus Therapeutics Inc.'s oral enzyme replacement therapy Galafold (migalastat) for the rare condition Fabry disease has enjoyed a strong initial launch in the US, Europe and Japan and the upward trajectory remains steep, largely thanks to the drug's relative ease of use, efficacy and price, according the the rare disease specialist's president.

Added sales momentum for Galafold could also come with better diagnosis of multiple sclerosis, "because Fabry can get mis-diagnosed as MS,"

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