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Rare Disease Roundtable: How Rare Is Too Rare?

 
• By Emily Hayes

Part 1: Execs from rare disease-focused companies weighed in on investor sentiment during a roundtable discussion led by Scrip at the J.P. Morgan Healthcare Conference.

Roundtabel participants seatedat table with Emily Hayes

With the help of regulatory incentives for orphan drugs, including additional exclusivity and priority review vouchers, drugs for rare diseases have become hot commodities.

Novartis AG' $8.7bn acquisition of the gene therapy company AveXis in April 2018 shows the degree of interest and value big pharmas place on treatments for rare conditions. (Also...

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