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BioMarin CEO Suggests Hemophilia Gene Therapy Pricing In $2m-$3m Range

 
• By Joseph Haas

During BioMarin’s earnings call Feb. 21, CEO Bienaime indicated the company may be looking to price its valoctocogene roxaparvovec gene therapy at $2m-$3m, as it would represent a savings over the annual cost of infused clotting factor therapy.

Dollar bills

The appropriate pricing of potentially curative gene therapies remains a contested question, but BioMarin Pharmaceutical Inc. seems ready to push a high boundary. Execs indicated during the firm’s earnings call Feb. 21 that it is looking to price the Phase III hemophilia A candidate valoctocogene roxaparvovec (BMN 270 or val-rox) at $2m-$3m, which would still represent savings compared to frequent infusions of Factor VIII therapies.

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