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UniQure Aiming To Be First With Hemophilia B Gene Therapy

Presenting 12 Month Data At ASH

 
• By Andrew McConaghie

The company has come a long way since gene therapy flop Glybera, and claims best-in-class status for viral vector.

uniQure
UniQure is headquartered in Amsterdam, the Netherlands • Source: UniQure

While BioMarin Pharmaceutical Inc. remains in pole position to be the first to bring the first hemophilia A gene therapy to market, uniQure has its sights on being the first in hemophilia B.

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