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Genentech’s SMA Type 1 Data Strengthen Case Backing Risdiplam Approval

 
• By Joseph Haas

With top-line data showing efficacy in type 1 SMA patients, risdiplam may be able to obtain a label that would address significantly more patients than Novartis’ Zolgensma. Final efficacy data will show how drug’s efficacy compares to Biogen’s Spinraza.

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Top-line data in type 1 SMA patients strengthens the case for risdiplam

With top-line, pivotal data showing efficacy in infants with type 1 spinal muscular atrophy (SMA), Genentech Inc. has bolstered the case for approval of risdiplam, a survival motor neuron-2 (SMN-2) splicing modifier under review at the US Food and Drug Administration with a 24 May action date.

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• By Dexter Jie Yan

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In Brief: BriaCell’s Breast Cancer Cell Therapy Boosts Survival In Phase II

 
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In Brief: BriaCell’s Breast Cancer Cell Therapy Boosts Survival In Phase II

 
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China’s Biotech Stocks Proved More Resilient Than US’s Amid Market Turmoil

 
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Henlius In David Versus Goliath Race With Pfizer For First PD-L1 ADC

 
• By Dexter Jie Yan

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