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Dynacure’s Antisense Approach To Rare Myopathies Gets Funding Boost

Ionis Collaborating On Development

 
• By John Davis

France’s fledgling biotech Dynacure has pulled together a series C funding round to support its ongoing Phase I/II study of an antisense molecule for an ultrarare myopathy.    

Skeletal_Muscle
Skeletal Muscle • Source: Shutterstock

Just four years after inception, the France/US rare diseases start-up Dynacure SAS has raised €50m ($55m) in a series C funding to help support an ongoing Phase I/II trial of its lead antisense candidate, DYN101, in patients with myotubular and centronuclear myopathies (CNMs).

As well as the ongoing trial in adults, the proceeds from the fundraising will also be used to expand the...

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