After Hemophilia Deal, UniQure Sees Zolgensma As Model For Huntington’s Gene Therapy

Focused On Long-Term Gene Therapy Leadership

While M&A-hungry investors were disappointed in no sale, uniQure now aims to pivot toward Huntington’s – and sees Zolgensma as an example to follow.

uniQure
uniQure had been tipped as a top M&A target for 2020

Gene therapy company uniQure NV may have disappointed investors hoping it would be the latest M&A target, but analysts have generally applauded its decision to take a different path.

Last week saw it strike a $450m upfront licensing deal for lead candidate, the Phase III hemophilia B gene therapy EtranaDez (formerly AMT-061) to blood disorders specialist CSL Behring

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