Amylyx Pharmaceuticals, Inc. had just three employees in early 2019, including co-CEOs/co-founders Justin Klee and Josh Cohen, and now the company is ready to submit its drug for regulatory approvals based on the Phase II/III CENTAUR clinical trial in amyotrophic lateral sclerosis (ALS), which showed slower disease progression for ALS patients treated with AMX0035 versus those who received a placebo.
Amylyx Drug Slows ALS Progression, Filings Imminent
Small Private Firm Plans To Commercialize On Its Own
Amylyx has raised just $75m to date, but that was enough to develop AMX0035 through a Phase II/III trial in which the drug slowed the progression of amyotrophic lateral sclerosis versus placebo.
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