Gene Therapies Must Bridge Gap Between Short-, Long-Term Efficacy

Sponsors for the three marketed gene therapies discussed lessons learned about acceptance and uptake of cell and gene therapies.

Drug makers have adopted or suggested a plethora of payment models for ensuring coverage of cell and gene therapies. But while they address the general question of how to pay for one-time therapies with exceptionally high upfront price tags, one issue that remains is how to factor in the availability of only short-term data.

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