Takeda Pharmaceutical Co. Ltd. is betting $100m, and potentially more than $1bn, on a start-up company that plans to develop in vivo gene therapies that would remove the need for patients to undergo stem cell collection or myeloablative conditioning, which could enable use of gene therapies in low-resource settings.
Ensoma Launches With Takeda Partnership On Myeloablation-Free Gene Therapy
The company also raised a $70m Series A round and is looking to develop “off-the-shelf” gene therapies adapted to settings with fewer resources.
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