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Orphazyme Tumbles Back To Earth As FDA Rejects Arimoclomol

Drug Turned Down For NPC

 
• By Kevin Grogan

Following a week of "insane trading" which saw the Danish stock soar based on social media chatter, US regulators have surprised the firm and investors by issuing a complete response letter for arimoclomol for Niemann-Pick disease type C.

Rollercoaster
The ups and downs of meme stocks • Source: Alamy

The rollercoaster ride for the so-called 'meme stock' Orphazyme A/S in the last week has come to a shuddering halt with shares in the Danish company crashing after US regulators rejected arimoclomol, its treatment for the ultra-rare disorder Niemann-Pick disease type C (NPC).

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