Landmark results from the first in vivo CRISPR gene-editing therapy have been unveiled by Intellia Therapeutics and Regeneron, and could put them at the forefront of a medical revolution.
Intellia Achieves Gene-Editing Breakthrough With First In Vivo CRISPR Therapy
Promise Of Safe And Effective Gene Editing Takes Step Forward
The first use of CRISPR/Cas9 in humans shows promising safety and efficacy against rare disease ATTR, and opens up the possibility of treating many genetic diseases.
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