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First Results From Editas CRISPR Eye Therapy Underwhelm Investors

Safety Is Reassuring But Efficacy Unclear

 
• By Andrew McConaghie

While rivals Intellia impressed with their first in vivo CRISPR gene-editing data, Editas’s first results in just two patients are not enough to convince investors.

Editas
Editas is one of a handful of biotechs developing in vivo CRISPR therapies, alongside the likes of Intellia and CRISPR Therapeutics • Source: Alamy

Shares in Editas Medicine have dropped 18% after the company shared the first results for EDIT-101, its CRISPR-based in vivo gene-editing treatment for rare eye disease Leber congenital amaurosis 10 (LCA10).

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• By Anju Ghangurde

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