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Orphazyme Teeters On The Brink As Arimoclomol File Is Pulled

NASDAQ Shares Delisted And Workforce Cut By 50%

 
• By Kevin Grogan

All hopes for survival rest on a meeting with the US FDA about arimoclomol now that the Danish biotech has withdrawn its submission for the Niemann-Pick disease type C therapy with the European Medicines Agency.

abyss
• Source: Alamy

Orphazyme A/S's annus horribilis is getting more horrible by the week and the latest setback has seen the beleaguered Danish biotech pull the file in Europe for arimoclomol, its investigational treatment for the ultra-rare disorder Niemann-Pick disease type C (NPC).

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