Encouraging Biomarker Data Lift UniQure’s Huntington’s Disease Hopes

Results Exceeded Expectations

Hopes rise as first four evaluable patients experienced no serious adverse events, and a sustained decline in level of key Huntington’s disease protein with the novel gene therapy product.

UniQure
The safety and biomarker data are encouraging, but it will take until 2023 before any potential disease modifying data are available. • Source: UniQure

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