Twin Intellia Readouts Further Bolster CRISPR Platform

The company presented interim data for NTLA-2002 in hereditary angioedema, along with interim data for Regeneron-partnered NTLA-2001 in transthyretin amyloidosis with cardiomyopathy. The company plans a rapid expansion of its programs.

Intellia announced data for NTLA-2002 and Regeneron-partnered NTLA-2001 • Source: Shutterstock

Intellia Therapeutics, Inc. is planning to further beef up its pipeline on the back of data for two of its in vivo CRISPR/Cas9 candidates, saying that the results provide further validation for its programs overall, in addition to setting the two candidates up as potentially competitive in their respective indications.

On 16 September, Intellia presented interim results from the Phase I/II study of NTLA-2002 in hereditary angioedema (HAE) at the 2022 Bradykinin Symposium in Berlin. It also announced interim results...

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