Busulfan-Induced Infertility May Deter Some Pediatric Patients From Bluebird, Other Gene Therapies

Partial Hold On Firm's Sickle Cell Therapy Lifted

Ovum preservation and sperm banking are options for post-puberty patients, but busulfan – used for myeloablative conditioning before certain gene therapies – may cause hesitation to use some treatments in children, experts at ASH told Scrip.

Bluebird said 19 December the FDA had lifted a partial hold on its lovo-cel trial • Source: Shutterstock

More from Gene Therapies

More from Advanced Therapies