BioMarin has hit a serious delay to agreeing a price for its hemophilia A gene therapy, Roctavian, in Germany, the product’s first global launch market.
BioMarin’s $1m Gene Therapy Roctavian Hits Payer Problems In Germany
Doubts About Blockbuster Prospects Linger
BioMarin has yet to treat a patient with Roctavian, the first ever hemophilia A gene therapy, eight months after its first approval in Europe, as pricing delays cloud its commercial prospects.
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