ASGCT Late Breakers: Pfizer’s Duchenne Results Underwhelm As Next-Gen Approaches Emerge

Sarepta Set For Landmark Approval

The congress’s late breakers highlight progress across cell and gene platforms and diseases, and Duchenne is in the spotlight as Sarepta’s SRP-9001 could soon gain accelerated approval.

LA Convention Center
An aerlal view of the L.A. Convenstion Center, the venue for this year's ASGCT annual congress. • Source: Shutterstock

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