ICER Report Assumes $2.8m Price For Libmeldy As Orchard Gears Up For US Debut

The drug-pricing watchdog gave the gene therapy for metachromatic leukodystrophy an “A” grade for use in presymptomatic patients receiving the therapy, which already is approved in Europe.

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The Institute for Clinical and Economic Review (ICER) issued a draft evidence report assessing the cost effectiveness of Orchard Therapeutics Limited’s gene therapy for metachromatic leukodystrophy (MLD) ahead of its US market debut, giving the product – already on the market in Europe – high marks in the treatment of presymptomatic patients but a lesser grade in the treatment of symptomatic children.

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