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Taysha’s Gene Therapy Steals Spotlight With Early Phase I/II Data In Rett Syndrome

Stock Up By 285%

 
• By Ayisha Sharma

The US biotech’s TSHA-102 has shown surprisingly early signs of functional improvement in a single patient treated in its Phase I/II Rett syndrome trial, promoting a major stock surge supported by the news of a $150 private placement and regulatory updates.  

different hands grabbing the air on blue background
Rett Syndrome Leads To Loss Of Both Gross And Fine Motor Skills • Source: Shutterstock

Taysha Gene Therapies, Inc.’ intrathecally delivered AAV9 gene therapy candidate, TSHA-102, has shown early promising motor function effects in a Phase I/II trial in Rett Syndrome, grabbing investor attention as the firm took steps to extend its cash runway.

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Pipeline Watch is a weekly snapshot of selected late-stage clinical trial events and approvals announced by pharmaceutical and biotech companies at medical and industry conferences, in financial and company presentations, and in company releases and statements.