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UniQure Downsizes Gene Therapy Ambitions, Pins Hopes On Huntington’s Data

 
• By Andrew McConaghie

Cutbacks to its workforce and early pipeline could help UniQure focus on core assets – but upcoming readouts to Huntington’s disease gene therapy will be key for investors.

UniQure

UniQure is to cut its workforce by 28% and drop more than half its research and technology projects in an effort to streamline and focus its gene therapy-based business.

The Amsterdam, Netherlands-headquartered firm will prioritize the continued development of AMT-130 in Huntington’s disease, which has been the focus of investor hopes for the company, but which posted mixed results from a US Phase I/II in June

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