There are no approved pharmacological therapies for congenital hearing loss and this situation is unlikely to change any time soon. Still, a glimmer of hope has been provided with signs of hearing improvement in a single patient with profound genetic deafness after treatment with Regeneron Pharmaceuticals, Inc.’s gene therapy, DB-OTO.
Regeneron Strikes A CHORD With Deafness Gene Therapy
A very early success with a gene therapy for a rare form of deafness puts Regeneron ahead of Lilly and Sensorion.
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