Verve Therapeutics's cholesterol lowering candidate, VERVE-101, has shown strong efficacy in its first Phase I study, representing a valuable proof-of-concept for its in vivo gene editing platform.
Verve’s Cholesterol Gene Editing Hits Milestone – With Lilly Now Onboard
The gene-editing company has achieved proof-of-concept for its base-editing platform in three patients – but safety concerns have sent its share price into decline.
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