Vertex and CRISPR Therapeutics have achieved a historic milestone with the approval of the first ever CRISPR/Cas9 based treatment, their sickle cell gene therapy and transfusion dependent beta-thalassemia treatment Casgevy.
Vertex Achieves Gene-Editing Milestone With First Ever CRISPR Therapy Approval
Great Britain is first to approve the groundbreaking CRISPR-based therapy for sickle cell and beta thalassemia. Vertex is yet to reveal its price, however, and wants to play down early expectations of its commercial potential.
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Pipeline Watch is a weekly snapshot of selected late-stage clinical trial events and approvals announced by pharmaceutical and biotech companies at medical and industry conferences, in financial and company presentations, and in company releases and statements.
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