France's Pharnext Undone By Placebo Effect

The Paris-based biotech's Charcot-Marie-Tooth disease drug falls short in Phase III.

Man Holding Up Falling Blocks
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Pharnext SA is reeling after the failure of its only late-stage asset PXT3003 less than a month after claiming that three companies were vying to partner the potential therapy for Charcot-Marie-Tooth disease.

The French biotech has unveiled topline results of a Phase III study (called PREMIER) of PXT3003, its drug candidate in Charcot-Marie-Tooth disease type 1A (CMT1A), a genetic disorder caused by...

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