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Sales Of BioMarin’s Hemophilia Gene Therapy Move At Glacial Pace

Three Patients Treated In 2023

 
• By Alaric DeArment

Analysts had forecast Q4 Roctavian sales of $5m-$6m, but they came in shy of $3m, and uptake has not yet come to reflect apparent demand.

• Source: Shutterstock

While BioMarin Pharmaceutical Inc.’s total fourth quarter and full year 2023 revenues rose from the comparable period in 2022, the launch of its hemophilia A gene therapy Roctavian (valoctocogene roxaparvovec-rvox) has been significantly slower than analysts had hoped, and the company suggested that uptake has not yet caught up with signs of market demand.

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