The drug development focus in Duchenne muscular dystrophy (DMD) has been on gene therapy recently, but Dyne Therapeutics is working to develop next-generation exon-skipping medications that would compete with Sarepta Therapeutics, Inc.’s established exon-skipping franchise, including Exondys 51 (eteplirsen).
Dyne Reports Progress Building Next-Generation Exon Skipping Franchise In DMD
The company reported updated data from the Phase I/II DELIVER trial testing DYNE-251 in patients with Duchenne muscular dystrophy (DMD) and announced leadership changes.
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