With a US Food and Drug Administration partial clinical hold lifted, Avidity Biosciences, Inc. is moving forward with a Phase III trial of its antibody-oligonucleotide conjugate (AOC) candidate delpacibart etedesiran (del-desiran, AOC 1001) that ultimately could bring the first approved therapy for myotonic dystrophy type 1 (DM1), a rare type of muscular dystrophy, to market.
With FDA Hold Lifted, Avidity Works To Bring First DM1 Therapy To Market
Avidity hopes to complete enrollment in mid-2025 for an ongoing Phase III trial of its antibody-oligonucleotide conjugate in myotonic dystrophy type 1, which has no approved drug therapy.
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Pipeline Watch is a weekly snapshot of selected late-stage clinical trial events and approvals announced by pharmaceutical and biotech companies at medical and industry conferences, in financial and company presentations, and in company releases and statements.
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