Jaguar Gene Therapy

After acquiring the neurodegenerative health-focused Prevail Therapeutics Inc. in late 2020 and further inking both a partnership and a financing commitment in the gene therapy space, Eli Lilly and

Applied Therapeutics Inc. has put a hold on a planned US filing for its galactosemia candidate, AT-007, because of a shift in US Food and Drug Administration approval parameters that means that bioma

Les Laboratoires Servier and fellow French firm Neurochlore 's efforts to develop the common diuretic bumetanide as a treatment for the symptoms of autism have floundered after they unveiled disappoi

BridgeBio Pharma, Inc. employs a business model of acquiring rights to or partnering with academic and institutional research in monogenic diseases and genetic cancer indications, often forming singl