Six- and seven-figure prices plus complicated administration and patient monitoring add up to difficult product launches for cell and gene therapies. Big pharma companies with novel medicines for hemophilia, cancer and other diseases are facing real-world challenges related to the cost and complexity of these products, which has made for slow initial uptake and measured sales growth.
Big Pharma Faces Cell And Gene Therapy Market Realities
Real-World Challenges For Novel Products
Big pharma executives at ARM’s Cell and Gene Meeting on the Mesa shared some of the practical challenges of bringing one-time treatments to market in hemophilia, cancer and beyond.

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